Guanidinylated neomycin delivers large, bioactive cargo into cells through a heparan sulfate-dependent pathway

J Biol Chem. 2007 May 4;282(18):13585-91. doi: 10.1074/jbc.M700463200. Epub 2007 Feb 20.

Abstract

Facilitating the uptake of molecules into living cells is of substantial interest for basic research and drug delivery applications. Arginine-rich peptides have been shown to facilitate uptake of high molecular mass cargos into cells, but the mechanism of uptake is complex and may involve multiple receptors. In this report, we show that a derivative of the aminoglycoside antibiotic neomycin, in which all of the ammonium groups have been converted into guanidinium groups, can carry large (>300 kDa) bioactive molecules across cell membranes. Delivery occurs at nanomolar transporter concentrations and under these conditions depends entirely on cell surface heparan sulfate proteoglycans. Conjugation of guanidinoneomycin to the plant toxin saporin, a ribosome-inactivating agent, results in proteoglycan-dependent cell toxicity. In contrast, an arginine-rich peptide shows both heparan sulfate-dependent and -independent cellular uptake. The high selectivity of guanidinoneomycin for heparan sulfate suggests the possibility of exploiting differences in proteoglycan compositions to target delivery to different cell types.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Animals
  • Biological Transport / drug effects
  • Biological Transport / physiology
  • CHO Cells
  • Cricetinae
  • Cricetulus
  • Dose-Response Relationship, Drug
  • Drug Delivery Systems*
  • Guanidine / analogs & derivatives
  • Guanidine / chemical synthesis
  • Guanidine / pharmacokinetics
  • Heparan Sulfate Proteoglycans / metabolism*
  • Membrane Glycoproteins / metabolism*
  • N-Glycosyl Hydrolases / pharmacokinetics
  • Neomycin / analogs & derivatives
  • Neomycin / chemical synthesis
  • Neomycin / pharmacokinetics*
  • Peptides / chemical synthesis
  • Peptides / pharmacokinetics
  • Plant Proteins / pharmacokinetics
  • Protein Binding / drug effects
  • Protein Synthesis Inhibitors / chemical synthesis
  • Protein Synthesis Inhibitors / pharmacokinetics*
  • Ribosome Inactivating Proteins, Type 1
  • Saporins

Substances

  • Heparan Sulfate Proteoglycans
  • Membrane Glycoproteins
  • Peptides
  • Plant Proteins
  • Protein Synthesis Inhibitors
  • Ribosome Inactivating Proteins, Type 1
  • N-Glycosyl Hydrolases
  • Saporins
  • Neomycin
  • Guanidine